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REDUCING NONSENSE-MEDIATED MRNA DECAY

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专利名称:REDUCING NONSENSE-MEDIATED MRNA

DECAY

发明人:Adrian Krainer,Isabel Aznarez,Tomoki

Nomakuchi

申请号:US14916561申请日:20140904

公开号:US20170159049A9公开日:20170608

摘要:The present disclosure relates to compositions and methods for inhibitingnonsense-mediated mRNA decay in a gene-specific manner, for example in the treatmentof diseases or disorders caused by nonsense mutations.

申请人:COLD SPRING HARBOR LABORATORY

地址:Cold Spring Harbor NY US

国籍:US

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